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Adeno-associated virus

Showing 1 - 25 of >10,000

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Menkes Syndrome Trial in Kunming (Recombinant adeno-associated virus administration)

Recruiting
  • Menkes Syndrome
  • Recombinant adeno-associated virus administration
  • Kunming, Yunnan, China
    Kunming Hope of Health Hospital
Aug 22, 2022

Hemophilia A Trial (Biospecimen Collection)

Not yet recruiting
  • Hemophilia A
  • Biospecimen Collection
  • (no location specified)
Oct 11, 2022

Seroprevalence and Seroconversion of Antibodies to

Recruiting
  • Hemophilia A
  • Blood sample collection
  • Madison, Wisconsin
    Covance Inc
Sep 16, 2022

Danon Disease Trial in La Jolla, Philadelphia (RP-A501)

Recruiting
  • Danon Disease
  • RP-A501
  • La Jolla, California
  • +1 more
Oct 17, 2023

Hemophilia B Trial (CSL222 (AAV5-hFIXco-Padua))

Not yet recruiting
  • Hemophilia B
  • CSL222 (AAV5-hFIXco-Padua)
  • (no location specified)
Aug 14, 2023

Idiopathic Parkinson's Disease Trial in United States (CERE-120 (Adeno-Associated Virus Serotype 2 [AAV2]-Neurturin [NTN]), Sham

Completed
  • Idiopathic Parkinson's Disease
  • CERE-120 (Adeno-Associated Virus Serotype 2 [AAV2]-Neurturin [NTN])
  • Sham Surgery
  • Birmingham, Alabama
  • +8 more
Nov 8, 2022

Achromatopsia Trial in Ann Arbor, London (adeno-associated virus vector AAV- CNGA3)

Completed
  • Achromatopsia
  • adeno-associated virus vector AAV- CNGA3
  • Ann Arbor, Michigan
  • +1 more
Feb 10, 2022

Hemophilia A, Gene Therapy Trial in Tianjin (Injection of GS001)

Recruiting
  • Hemophilia A
  • Gene Therapy
  • Injection of GS001
  • Tianjin, Tianjin, China
    Chinese Academy of Medical Science and Blood Disease Hospital
Sep 19, 2022

Pompe Disease Infantile-Onset Trial in China (GC301)

Not yet recruiting
  • Pompe Disease Infantile-Onset
  • GC301
  • Beijing, China
  • +4 more
Apr 2, 2023

Retinal Disease, Retinitis Pigmentosa Trial in Riyadh (Subretinal administration of rAAV2-VMD2-hMERTKRecombinant

Completed
  • Retinal Disease
  • Retinitis Pigmentosa
  • Subretinal administration of rAAV2-VMD2-hMERTKRecombinant Adeno-Associated Virus
  • Riyadh, Saudi Arabia
    King Khaled Eye Specialist Hospital
Jan 25, 2022

Infantile-onset Pompe Disease Trial in Beijing (Genetic: GC301)

Recruiting
  • Infantile-onset Pompe Disease
  • Genetic: GC301
  • Beijing, Beijing, China
    Bayi Children's Hospital, Seventh Medical Center, PLA general ho
Sep 30, 2022

Severe Hemophilia A Subjects Who Received BMN 270 inPrior

Enrolling by invitation
  • Hemophilia A
    • London, United Kingdom
      Royal London Hospital, Barts and the London Hemophilia Center
    Mar 13, 2023

    Parkinson's Disease Trial run by the National Institute of Neurological Disorders and Stroke (NINDS) (Convection enhanced

    Completed
    • Parkinson's Disease
    • Convection enhanced delivery/AAV2-GDNF
    • Bethesda, Maryland
      National Institutes of Health Clinical Center
    Jan 26, 2023

    Pompe Disease Trial in Gainesville (genetic, drug, other)

    Completed
    • Pompe Disease
    • Recombinant Adeno-Associated Virus Acid Alpha-Glucosidase
    • +7 more
    • Gainesville, Florida
      Clinical and Translational Research Building (CTRB), University
    Mar 24, 2022

    Friedreich Ataxia, Cardiomyopathies, Cardiac Hypertrophy Trial in New York (AAVrh.10hFXN, serotype rh.10 adeno-associated virus

    Recruiting
    • Friedreich Ataxia
    • +3 more
    • AAVrh.10hFXN, serotype rh.10 adeno-associated virus (AAV) gene transfer vector expressing the cDNA coding for human FXN
    • Prednisone
    • New York, New York
      Weill Cornell Medicine
    Jul 15, 2022

    Glycogen Storage Disease Type IA Trial in Worldwide (genetic, other, drug)

    Recruiting
    • Glycogen Storage Disease Type IA
    • DTX401
    • +3 more
    • Orange, California
    • +16 more
    Jan 13, 2023

    Parkinson's Disease Trial in San Francisco, Chicago (CERE-120: AAV2-NTN)

    Completed
    • Parkinson's Disease
    • CERE-120: AAV2-NTN
    • San Francisco, California
    • +1 more
    Nov 8, 2022

    Adeno-Associated Virus Antibody Study in Subjects OTC

    Recruiting
    • Ornithine Transcarbamylase Deficiency
    • +2 more
      • Akron, Ohio
      • +2 more
      Jul 22, 2022

      Retinitis Pigmentosa Trial in New York (BS01)

      Recruiting
      • Retinitis Pigmentosa
      • New York, New York
        OCLI
      Nov 2, 2021

      PKP2 Arrhythmogenic Cardiomyopathy (PKP2-ACM) Trial in La Jolla, Philadelphia (RP-A601)

      Not yet recruiting
      • PKP2 Arrhythmogenic Cardiomyopathy (PKP2-ACM)
      • RP-A601
      • La Jolla, California
      • +1 more
      May 22, 2023

      Squamous Cell Head Neck Cancer, Radiation Induced Xerostomia, Salivary Hypofunction Trial run by the (AAV2hAQP1)

      Recruiting
      • Squamous Cell Head and Neck Cancer
      • +2 more
      • AAV2hAQP1
      • Bethesda, Maryland
        National Institutes of Health Clinical Center, 9000 Rockville Pi
      May 3, 2022

      Hemophilia B Trial in Tianjin (Single dose intravenous injection of BBM-H901)

      Active, not recruiting
      • Hemophilia B
      • Single dose intravenous injection of BBM-H901
      • Tianjin, Tianjin, China
        Institute of Hematology & Blood Diseases Hospital
      Dec 12, 2021

      Alpha 1-Antitrypsin Deficiency Trial in Gainesville, Charleston (ADVM-043)

      Completed
      • Alpha 1-Antitrypsin Deficiency
      • ADVM-043
      • Gainesville, Florida
      • +1 more
      Aug 3, 2022

      Long Term Follow-Up Gene Therapy Study for XLRP RPGR

      Recruiting
      • X-Linked Retinitis Pigmentosa
      • AAV-RPGR
      • Boston, Massachusetts
      • +3 more
      Dec 5, 2022

      Canavan Disease Trial in Boston (AAV9 BBP-812)

      Recruiting
      • Canavan Disease
      • AAV9 BBP-812
      • Boston, Massachusetts
        Massachusetts General Hospital (MGH); Center for Rare Neurologic
      Mar 12, 2022