Adeno-associated virus
Showing 1 - 25 of >10,000
Menkes Syndrome Trial in Kunming (Recombinant adeno-associated virus administration)
Recruiting
- Menkes Syndrome
- Recombinant adeno-associated virus administration
-
Kunming, Yunnan, ChinaKunming Hope of Health Hospital
Aug 22, 2022
Hemophilia A Trial (Biospecimen Collection)
Not yet recruiting
- Hemophilia A
- Biospecimen Collection
- (no location specified)
Oct 11, 2022
Seroprevalence and Seroconversion of Antibodies to
Recruiting
- Hemophilia A
- Blood sample collection
-
Madison, WisconsinCovance Inc
Sep 16, 2022
Danon Disease Trial in La Jolla, Philadelphia (RP-A501)
Recruiting
- Danon Disease
- RP-A501
-
La Jolla, California
- +1 more
Oct 17, 2023
Hemophilia B Trial (CSL222 (AAV5-hFIXco-Padua))
Not yet recruiting
- Hemophilia B
- CSL222 (AAV5-hFIXco-Padua)
- (no location specified)
Aug 14, 2023
Idiopathic Parkinson's Disease Trial in United States (CERE-120 (Adeno-Associated Virus Serotype 2 [AAV2]-Neurturin [NTN]), Sham
Completed
- Idiopathic Parkinson's Disease
- CERE-120 (Adeno-Associated Virus Serotype 2 [AAV2]-Neurturin [NTN])
- Sham Surgery
-
Birmingham, Alabama
- +8 more
Nov 8, 2022
Achromatopsia Trial in Ann Arbor, London (adeno-associated virus vector AAV- CNGA3)
Completed
- Achromatopsia
- adeno-associated virus vector AAV- CNGA3
-
Ann Arbor, Michigan
- +1 more
Feb 10, 2022
Hemophilia A, Gene Therapy Trial in Tianjin (Injection of GS001)
Recruiting
- Hemophilia A
- Gene Therapy
- Injection of GS001
-
Tianjin, Tianjin, ChinaChinese Academy of Medical Science and Blood Disease Hospital
Sep 19, 2022
Pompe Disease Infantile-Onset Trial in China (GC301)
Not yet recruiting
- Pompe Disease Infantile-Onset
- GC301
-
Beijing, China
- +4 more
Apr 2, 2023
Retinal Disease, Retinitis Pigmentosa Trial in Riyadh (Subretinal administration of rAAV2-VMD2-hMERTKRecombinant
Completed
- Retinal Disease
- Retinitis Pigmentosa
- Subretinal administration of rAAV2-VMD2-hMERTKRecombinant Adeno-Associated Virus
-
Riyadh, Saudi ArabiaKing Khaled Eye Specialist Hospital
Jan 25, 2022
Infantile-onset Pompe Disease Trial in Beijing (Genetic: GC301)
Recruiting
- Infantile-onset Pompe Disease
- Genetic: GC301
-
Beijing, Beijing, ChinaBayi Children's Hospital, Seventh Medical Center, PLA general ho
Sep 30, 2022
Severe Hemophilia A Subjects Who Received BMN 270 inPrior
Enrolling by invitation
- Hemophilia A
-
London, United KingdomRoyal London Hospital, Barts and the London Hemophilia Center
Mar 13, 2023
Parkinson's Disease Trial run by the National Institute of Neurological Disorders and Stroke (NINDS) (Convection enhanced
Completed
- Parkinson's Disease
- Convection enhanced delivery/AAV2-GDNF
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Jan 26, 2023
Pompe Disease Trial in Gainesville (genetic, drug, other)
Completed
- Pompe Disease
- Recombinant Adeno-Associated Virus Acid Alpha-Glucosidase
- +7 more
-
Gainesville, FloridaClinical and Translational Research Building (CTRB), University
Mar 24, 2022
Friedreich Ataxia, Cardiomyopathies, Cardiac Hypertrophy Trial in New York (AAVrh.10hFXN, serotype rh.10 adeno-associated virus
Recruiting
- Friedreich Ataxia
- +3 more
- AAVrh.10hFXN, serotype rh.10 adeno-associated virus (AAV) gene transfer vector expressing the cDNA coding for human FXN
- Prednisone
-
New York, New YorkWeill Cornell Medicine
Jul 15, 2022
Glycogen Storage Disease Type IA Trial in Worldwide (genetic, other, drug)
Recruiting
- Glycogen Storage Disease Type IA
- DTX401
- +3 more
-
Orange, California
- +16 more
Jan 13, 2023
Parkinson's Disease Trial in San Francisco, Chicago (CERE-120: AAV2-NTN)
Completed
- Parkinson's Disease
- CERE-120: AAV2-NTN
-
San Francisco, California
- +1 more
Nov 8, 2022
Adeno-Associated Virus Antibody Study in Subjects OTC
Recruiting
- Ornithine Transcarbamylase Deficiency
- +2 more
-
Akron, Ohio
- +2 more
Jul 22, 2022
PKP2 Arrhythmogenic Cardiomyopathy (PKP2-ACM) Trial in La Jolla, Philadelphia (RP-A601)
Not yet recruiting
- PKP2 Arrhythmogenic Cardiomyopathy (PKP2-ACM)
- RP-A601
-
La Jolla, California
- +1 more
May 22, 2023
Squamous Cell Head Neck Cancer, Radiation Induced Xerostomia, Salivary Hypofunction Trial run by the (AAV2hAQP1)
Recruiting
- Squamous Cell Head and Neck Cancer
- +2 more
- AAV2hAQP1
-
Bethesda, MarylandNational Institutes of Health Clinical Center, 9000 Rockville Pi
May 3, 2022
Hemophilia B Trial in Tianjin (Single dose intravenous injection of BBM-H901)
Active, not recruiting
- Hemophilia B
- Single dose intravenous injection of BBM-H901
-
Tianjin, Tianjin, ChinaInstitute of Hematology & Blood Diseases Hospital
Dec 12, 2021
Alpha 1-Antitrypsin Deficiency Trial in Gainesville, Charleston (ADVM-043)
Completed
- Alpha 1-Antitrypsin Deficiency
- ADVM-043
-
Gainesville, Florida
- +1 more
Aug 3, 2022
Long Term Follow-Up Gene Therapy Study for XLRP RPGR
Recruiting
- X-Linked Retinitis Pigmentosa
- AAV-RPGR
-
Boston, Massachusetts
- +3 more
Dec 5, 2022
Canavan Disease Trial in Boston (AAV9 BBP-812)
Recruiting
- Canavan Disease
- AAV9 BBP-812
-
Boston, MassachusettsMassachusetts General Hospital (MGH); Center for Rare Neurologic
Mar 12, 2022